This is a list of investigational acne drugs, or drugs that are currently under development for clinical use in the treatment of acne but are not yet approved.
Chemical/generic names are listed first, with developmental code names, synonyms, and brand names in parentheses. The format of list items is "Name (Synonyms) â Mechanism of Action [Reference]".
This list was last comprehensively updated in September 2025. It is likely to become outdated with time.
Under development
Phase 3
Phase 2/3
- B-244 (AOB-101; AOB-102; AOB-103; AOB-201; AOB-202; AOB-203; B244; nitrosomonas eutropha D23) â bacteria replacement
Phase 2
- Acetylcysteine lysinate (L-lysine-N-acetyl-L-cysteinate; N-acetylcysteine lysinate; Nacystelyn) â antioxidant
- Aminolevulinic acid (ALA; BF-200 ALA) â photosensitizer
- Cannabidiol topical (CBD; BTX-1204; BTX-1308; BTX-1503; BTX-1702; BTX-1801; PBX-1308) â cannabinoid
- Dimethylcurcumin (ASCJ-9; AJ-101; ASC-J9) â androgen receptor degradation enhancer
- Imsidolimab (ANB-019) â monoclonal antibody against the interleukin-36 receptor
- Ivermectin topical (CD-5024; Soolantra) â non-mammalian chloride channel opener
- LYS-006 â leukotriene A4 hydrolase (LTA4H) inhibitor
- Methyl aminolevulinate (MAL; CD06809-41; Luxerm; MAL-PDT; Metvix; Metvixia; P-1202; Visonac) â photosensitizer
- NAI Acne (BI-Acne; BI-K-0376; CB-06-01; CB-06-04; NAI-003; NAI-Acne; VIC-acne) â peptide elongation factor Tu inhibitor
- Omiganan (CLS-001; CPI-226; MBI-226; MBI-594AN; MX-226; MX-594AN; Omigard) â antiseptic/antibacterial
- Pyrilutamide (EX-A5504; HY-145451; KXâÂÂ826) â antiandrogen (androgen receptor antagonist)
- Tretinoin topical â retinoid (retinoic acid receptor agonist)
- VB-1953 â antibiotic and toll-like receptor antagonist
Phase 1/2
Phase 1
- AMTX-100 â transcription factor modulator
- ASC-60 (TVB-3567) â fatty acid synthetase complex inhibitor
- Trifarotene â retinoic acid receptor gamma (RAR-ó) agonist
Preclinical
- Acne vaccine â immunostimulant
- ADA-308 â antiandrogen (androgen receptor antagonist)
- Research programme: acne vulgaris therapeutics - Attillaps Pharmaceuticals â acetylcholinesterase inhibitors
Research
- Topical acne vulgaris therapeutic (novel compound 8) â undefined mechanism of action
Not under development
No development reported
- Adapalene/minocycline (FCD-105) â combination of adapalene (retinoid) and minocycline (tetracycline antibiotic)
- Auriclosene (AgaDerm; AgaNase; AL-46383A; CD-07223; DCDMT; NVC-422) â aganocide compound and antimicrobial
- Bermekimab (CA-18C3; CV-18C3; Hutruo; JNJ-77474462; MAB-p1; RA-18C3; T2-18C3; Xilonix) â monoclonal antibody against interleukin-1ñ
- BOS-356 (GSK-3008356) â diacylglycerol O-acyltransferase inhibitor
- Brilacidin (PMX-30063) â host defense protein (HDP) mimetic antibiotic
- Carbamide peroxide topical (E-0301) â disinfectant and bleaching agent
- CJM-112 â IL17A and IL17F inhibitor
- Clindamycin/tretinoin â combination of clindamycin (lincosamide antibiotic) and tretinoin (retinoid)
- Clindamycin/tretinoin â combination of clindamycin (lincosamide antibiotic) and tretinoin (retinoid)
- DMT-200 (DMT-210; DMT-220; SIG-990) â isoprenylcysteine analogue and various actions
- Estradiol valerate/dienogest (Climodien; Climodiène; Klimodien; Lafamme) â combination of estradiol valerate (estrogen) and dienogest (progestogen)
- Ethinylestradiol/chlormadinone acetate (Balianca; Belara; GRT4248) â combination of ethinylestradiol (estrogen) and chlormadinone acetate (progestogen) and a combined oral contraceptive
- Ethinylestradiol/drospirenone (Petibelle; SH-470; Yasmin; ZK-30595) â combination of ethinylestradiol (estrogen) and drospirenone (progestogen)
- GSK-1940029 â stearoyl-CoA desaturase inhibitor
- GT-20029 (AR-PROTAC) â androgen receptor degradation enhancer
- IP10-C8 â CD13 antigen inhibitor and dipeptidyl peptidase 4 (DPP4) inhibitor
- Minocycline extended release (Emrosi; Ximino) â tetracycline antibiotic
- Minocycline topical (HY01) â tetracycline antibiotic
- MTC-896 â melanocortin receptor antagonist
- Nitric oxide (Enovid; FabiSpray; NORS-0791; NORS-1002; NORS-2791; NORS-4002; NORS-6491; NORS) â nitric oxide donor
- ORG-101 (acne vulgaris vaccine; ORI-001; ORI-A-ce001) â immunostimulant, vaccine
- Radezolid (RX-01667; Rx-01_667; RX-103; RX-1741) â oxazolidone antibiotic
- Research programme: antimicrobial therapies - NovaBiotics â cell membrane permeability enhancers
- Research programme: synthetic cannabinoid therapeutics - Claritas Pharmaceuticals â cannabinoids (cannabinoid receptor modulators)
- Research programme: therapeutic antibody fragments - Kuur Therapeutics â various actions
- Silver dihydrogen citrate (SDC; Axenohl) â antiseptic/antibacterial
- Tazarotene topical (DFD-03) â retinoid X receptor agonist
Discontinued
- Acebilustat (CTX-4430; EP-501) â leukotriene A4 (LTA4H) hydrolase inhibitor
- Afamelanotide (CUV-1647; EPT-1647; Melanotan I; Melanotan; Prenumbra; Scenesse) â melanocortin receptor agonist
- BBI-3000 â retinoid X receptor agonist
- BMX-010 (MnTE-2-PyP) â reactive oxygen species (ROS) scavenger and radioprotector
- Botulinum toxin A liquid (AI-09) â acetylcholine release inhibitor and neuromuscular blocking agent
- Botulinum toxin A topical (ANT-1207) â acetylcholine release inhibitor and neuromuscular blocking agent
- Cioteronel (CPC-10997; Cyoctol; X-Andron) â antiandrogen (androgen receptor antagonist)
- Diroleuton (DGLA; DHLA; DS-107; RO-12-1989) â omega-6 fatty acid and anti-inflammatory
- DMVT-503 (RVT-503) â undefined mechanism of action
- DX-0385 â retinoic acid metabolism modulator
- Encapsulated tretinoin cream â retinoid (retinoic acid receptor agonist)
- Epristeride (Aipuliete; ONO-9302; SKF-105657) â 5ñ-reductase inhibitor
- Falecalcitriol (DSC-103; F6VD3; flocalcitriol; Fulstan; hexafluorocalcitriol; hexafluorovitamin D3; Hornel; SM-8000; ST-630) â vitamin D/calcitriol analogue
- Gevokizumab (S-78989; VPM-087; XMA-005.2) â monoclonal antibody against interleukin-1ò
- Hypochlorous acid (PR-013; PR-022) â disinfectant and other actions
- Imsidolimab (ANB-019) â monoclonal antibody against the interleukin-36 receptor
- Incyclinide (chemically modified tetracycline 3; CMT-3; COL-3; Metastat) â chemically modified tetracycline and matrix metalloproteinase inhibitor (no antibiotic activity)
- Ingenol disoxate (LEO-43204) â undefined mechanism of action
- JNJ-10229570 â melanocortin MC<sub>5</sub> receptor antagonist
- MDI-301 â undefined mechanism of action
- MK-434 (MK-0434) â 5ñ-reductase inhibitor
- MTCH-24 (Zilex; Zorex) â undefined mechanism of action
- PF-06423264 â acetyl-CoA carboxylase inhibitor
- PSK-3841 (HMR-3841; RU-58841) â antiandrogen (androgen receptor antagonist)
- Research programme: acne therapeutics - Praxis â undefined mechanism of action
- Research programme: tetracycline derivatives - Paratek Pharmaceuticals (P-004292) â tetracycline derivatives
- Rose bengal sodium (PH-10; Provecta; PV-10; rose bengal; Xantryl) â immunomodulator and other actions
- Santalum album ointment (albuterpenoid; East Indian sandalwood oil) â undefined mechanism of action
- Talarozole (R115866; Rambazole) â retinoic acid metabolism modulator
- Thykamine (PCT-233; PUR-0110) â undefined mechanism of action (anti-inflammatory)
- Valproic acid topical (Avugane; Baceca; G2M-777) â histone deacetylase inhibitor and other actions
- XEN-801 (XEN801) â stearoyl-CoA desaturase inhibitor
- XOMA-629 (XMP-629) â endotoxin inhibitor
- Zileuton (A-64077; Abbott-64077; ABT-077; CRTX-073; CTI-02; Zyflo) â 5-lipoxygenase inhibitor
Not under development
- Isotretinoin topical â retinoid (retinoic acid receptor agonist)
Clinically used drugs
Approved drugs
Single-drug formulations
- Adapalene (CD-271; Differin) â retinoid (retinoic acid receptor agonist)
- Azelaic acid (BAY39-6251; Finacea; Skinoren) â undefined mechanism of action
- Benzoyl peroxide (Bepio; M6050; M605101) â undefined mechanism of action
- Clascoterone (Breezula; Winlevi; CB-03-01; cortexolone 17ñ-propionate) â antiandrogen (androgen receptor antagonist)
- Clindamycin (ResiDerm A; Zindaclin) â lincosamide antibiotic
- Dapsone topical (Aczone; Atrisone) â sulfone antibiotic
- Doxycycline hyclate (Acticlate; Monodox; AQ101) â tetracycline antibiotic
- Isotretinoin (Absorica; Accutane; CIP-isotretinoin; Epuris; Lisacne-CIP) â retinoid (retinoic acid receptor agonist)
- Minocycline (DFD-10; DFD-29; Emrosi; Minolira) â tetracycline antibiotic
- Minocycline foam (Amzeeq; FMX-102; FMX-103; FMX-101; FXFM-244; Zilxi) â tetracycline antibiotic
- Nadifloxacin topical â fluoroquinolone antibiotic
- Ozenoxacin (Dubine; GF-001001-00; M-5120; M-512101; M-512102; Ozadub; Ozanex; T-3912; Xepi; Zebiax) â quinolone antibiotic
- Sarecycline (Seysara; P-0005672; WC-3035) â narrow-spectrum tetracycline antibiotic
- Solubilised benzoyl peroxide (CLENZIderm M.D.; SoluCLENZ Rx Gel) â undefined mechanism of action
- Tazarotene topical (AGN-190299; Avage; Fabior; Suretin; Tazorac; Zorac) â retinoid (retinoic acid receptor agonist)
- Tretinoin (Acnisdin Retinoico; All-trans retinoic acid; Arotinoid; Avita; Dermojuventus; Loderm Retinoico; NSC 122758; Retinoic acid; Retirides; Vesanoid; Vitamin A acid; Vitamin-A Acid; Vitanol) â retinoid (retinoic acid receptor agonist)
- Tretinoin lotion (Altreno; IDP-121) â retinoid (retinoic acid receptor agonist)
- Trifarotene (Aklief; CD-5789) â retinoid acid receptor gamma (RAR-ó) agonist
Combination formulations
Off-label drugs
- Antihistamines (histamine H<sub>1</sub> receptor antagonists) (e.g., cetirizine, desloratadine, fexofenadine, levocetirizine, loratadine)
- Corticosteroids (corticosteroid receptor agonists) (e.g., hydrocortisone, prednisone, triamcinolone acetonide)
- Hydroquinone â tyrosinase inhibitor and skin-lightening agent
- Nicotinamide (niacinamide) â vitamin B<sub>3</sub>
- Oral antiandrogens (androgen receptor antagonists) (e.g., spironolactone, cyproterone acetate, flutamide, bicalutamide, ketoconazole, cimetidine)
- Other antibiotics (e.g., erythromycin, metronidazole, sulfacetamide)
- Other ethinylestradiol-containing combined oral contraceptives
- Salicylic acid â various actions (keratolytic, comedolytic, and bacteriostatic)
- Zinc â undefined mechanism of action (antibacterial and anti-inflammatory)
See also
References
External links