List of gene therapies

This article contains a list of commercially available gene therapies.

Gene therapies

• Alipogene tiparvovec (Glybera): AAV-based treatment for lipoprotein lipase deficiency (no longer commercially available)
• Axicabtagene ciloleucel (Yescarta): treatment for large B-cell lymphoma
• Beremagene geperpavec (Vyjuvek): treatment of wounds.
• Betibeglogene autotemcel (Zynteglo): treatment for beta thalassemia
• Brexucabtagene autoleucel (Tecartus): treatment for mantle cell lymphoma and acute lymphoblastic leukemia
• Cambiogenplasmid (Neovasculgen): treatment for vascular endothelial growth factor peripheral artery disease
• Ciltacabtagene autoleucel (Carvykti): treatment for multiple myeloma
• Delandistrogene moxeparvovec (Elevidys): treatment for Duchenne muscular dystrophy
• Elivaldogene autotemcel (Skysona): treatment for cerebral adrenoleukodystrophy
• Etranacogene dezaparvovec (Hemgenix): AAV-based treatment for hemophilia B
• Exagamglogene autotemcel (Casgevy): treatment for sickle cell disease.
• Gendicine: treatment for head and neck squamous cell carcinoma
• Idecabtagene vicleucel (Abecma): treatment for multiple myeloma
• Lovotibeglogene autotemcel (Lyfgenia): treatment for sickle cell disease.
• Nadofaragene firadenovec (Adstiladrin): treatment for bladder cancer
• Obecabtagene autoleucel (Aucatzyl): treatment of acute lymphoblastic leukemia
• Onasemnogene abeparvovec (Zolgensma): AAV-based treatment for spinal muscular atrophy
• Prademagene zamikeracel (Zevaskyn): recessive dystrophic epidermolysis bullosa
• Revakinagene taroretcel (Encelto): treatment of macular telangiectasia type 2
• Strimvelis: treatment for adenosine deaminase deficiency (ADA-SCID)
• Talimogene laherparepvec (Imlygic): treatment for melanoma in people who have recurring skin lesions
• Tisagenlecleucel (Kymriah): treatment for B cell lymphoblastic leukemia
• Valoctocogene roxaparvovec (Roctavian): treatment for hemophilia A
• Voretigene neparvovec (Luxturna): AAV-based treatment for Leber congenital amaurosis

See also

• FDA-approved CAR T cell therapies

References

External links